Gene therapy for sickle cell disease passes key preclinical test — Harvard Gazette

A precision-engineered gene therapy virus, inserted into blood stem cells that are then transplanted, markedly reduced sickle-induced red-cell damage in mice with sickle cell disease, researchers from Dana-Farber/Boston Children’s Cancer and Blood Disorders Center reported in the Journal of Clinical Investigation.

New study shows promising evidence for sickle cell gene therapy - UChicago Medicine

gene therapy, The Stem Cellar

gene therapy, The Stem Cellar

Gene therapy for sickle cell disease passes key preclinical test — Harvard Gazette

Денис Савин (@withoutpassions) / X

PDF) Editing Human DNA Moral and social implications of germline genetic modification

PDF) Editing Human DNA Moral and social implications of germline genetic modification

A systematic review of quality of life in sickle cell disease and thalassemia after stem cell transplant or gene therapy - ScienceDirect

Frontiers Genome editing for sickle cell disease: still time to correct?

Sickle Cell Anemia and Gene Therapy: How It Works

SEC Filing CRISPR Therapeutics